Niemann Pick Type C Disease clinical trials

Explore recruiting niemann pick type c disease clinical trials.

Recruiting niemann pick type c disease studies right now

Study details & eligibility ClinicalTrials.gov record

Also recruiting in Europe

Niemann Pick Type C Disease trials registered in the EU Clinical Trials Information System (CTIS). These are outside the "near me" matcher above - open a study for full details.

18-month double-blind, randomized, placebo-controlled, multicenter, Phase 3 study to evaluate the safety and efficacy of oral nizubaglustat (AZ-3102) in late-infantile and juvenile forms of Niemann-Pick type C disease and in late-infantile and juvenile-onset forms of GM1 gangliosidosis or GM2 gangliosidosis

France, Portugal, Germany, Italy, Spain, Sweden

Therapeutic confirmatory (Phase III) EU CTIS Study details

Niemann Pick Type C Disease trials by city

Niemann Pick Type C Disease clinical trials

Recruiting niemann pick type c disease studies right now

A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease, GM1 Gangliosidosis or GM2 Gangliosidosis

A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease

UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Retinal Hyperspectral Imaging in Neurodegenerative Diseases

A Pivotal Study of N-Acetyl-L-Leucine on Niemann-Pick Disease Type C

A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of Niemann-Pick Type C Disease (NPC)

A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile Forms of GM1 Gangliosidosis or GM2 Gangliosidosis

Also recruiting in Europe

Niemann Pick Type C Disease trials by city

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