Mucopolysaccharidosis Type I Hurler clinical trials

Explore recruiting mucopolysaccharidosis type i hurler clinical trials.

Recruiting mucopolysaccharidosis type i hurler studies right now

Study details & eligibility ClinicalTrials.gov record
Study details & eligibility ClinicalTrials.gov record

Also recruiting in Europe

Mucopolysaccharidosis Type I Hurler trials registered in the EU Clinical Trials Information System (CTIS). These are outside the "near me" matcher above - open a study for full details.

A phase I/II study evaluating safety and efficacy of autologous hematopoietic stem and progenitor cells genetically modified with IDUA lentiviral vector encoding for the human α-L-iduronidase gene for the treatment of patients affected by Mucopolysaccharidosis Type I, Hurler variant

Italy

Phase I and Phase II (Integrated)- First administration to humans EU CTIS Study details

A multi-center, randomized, active controlled clinical trial to evaluate the efficacy and safety of OTL-203 in subjects with mucopolysaccharidosis type I, Hurler syndrome (MPS-IH) compared to standard of care with allogeneic hematopoietic stem cell transplantation (allo-HSCT)

Italy, Netherlands

Therapeutic confirmatory (Phase III) EU CTIS Study details

Mucopolysaccharidosis Type I Hurler trials by city

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