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New treatment option for Congenital Myasthenic Syndrome
Official title Patients With Congenital Myasthenic Syndrome Will be Treated With Mesenchymal Stem Cell Exosome Solution
ClinicalTrials.gov ID: NCT07226726
What this study is testing
What is AlloEx exosomes?
AlloEx exosomes is an investigational medicine, being studied as a potential treatment for congenital myasthenic syndrome.
Plain-language explanation of the investigational treatment - it is being studied and is not an approved or proven therapy. The study team can confirm the details.
- What it's testing
- Patients with Congenital Myasthenic Syndrome will be treated with Mesenchymal Stem Cell Exosome solution.
- Phase 1: an early, usually small safety study
A plain-language read of the study's public ClinicalTrials.gov listing. The study team confirms the details.
Who can take part
Ages 18 and older
You may be able to join if
- Patients will need a diagnosis of Congenital Myasthenic Syndrome by a licensed physician.
- Patients must be able to provide informed consent, or have a guardian who does.
- Patient must be able to travel to the site of treatment.
You likely can't join if
- Patients will be excluded from the trial if they are pregnant or have active cancer (malignancy) at the screening consultation.
The study team makes the final eligibility decision.
Where it's taking place
- Naples, Florida, United States
- Irving, Texas, United States
- St John's, Antigua and Barbuda
Questions & answers
Do participants get paid in this trial?
This listing doesn't specify compensation. Many trials still reimburse travel or offer a stipend, so it's worth asking the study team when you connect.
Is it free to join, and do I need insurance?
Searching and applying through BridgeMD is free. In clinical trials the study-related treatment and visits are generally provided at no cost to you. You usually don't need insurance to take part - confirm specifics with the study team.
How long does this study last?
The listing doesn't state an exact length. The study team walks you through the schedule and number of visits before you decide to enroll.
Who can join this trial?
This study is enrolling all sexes, 18 years and older. The study team makes the final eligibility decision.
Where is this trial taking place?
Study sites include Naples, Florida, United States; Irving, Texas, United States; St John's, Antigua and Barbuda. Enter your location above to see the nearest site and check your eligibility.
Explore other conditions
BridgeMD is an information and trial-matching tool - not medical advice, and not the study sponsor. Details come from ClinicalTrials.gov; the study team decides eligibility.