BridgeMD
New treatment option for Myotonic Dystrophy, Congenital
Official title Music Intervention for Brain-Heart Disease in Myotonic Dystrophy Type 1 (DM1)
ClinicalTrials.gov ID: NCT06809049
What this study is testing
- What it's testing
- The goal of this interventional study is to demonstrate the feasibility and tolerability of music and movement intervention for children with congenital DM1, while providing indications of its effectiveness in improving brain and heart symptoms of DM1. Additionally, information from the collection of biological samples and wearable devices (accelerometer, EEG headband and ECG chest strap) will be used to identify brain-heart biomarkers and outcome measures for use in future research and trials.
A plain-language read of the study's public ClinicalTrials.gov listing. The study team confirms the details.
Who can take part
Ages 6 to 18
You may be able to join if
- Participants between the ages of 6 to 18 with genetically confirmed congenital or infantile-onset myotonic dystrophy type 1 (DM1).
- Participants willing to stay on stable medication from the day of screening to end of study.
You likely can't join if
- Insufficient English language skills to complete required assessments and questionnaires.
- Participant is non-verbal.
- Failure to provide signed informed consent by participant or designated decision maker (i.e. parent, legal guardian or power of attorney).
- Failure to provide signed informed consent by parents/caregivers for dyad participation.
- Participant is not a resident of Canada, due to risk of attrition.
- Patients for whom - in the opinion of the investigator - it would not be safe to participate in the study.
The study team makes the final eligibility decision.
Where it's taking place
- Ottawa, Ontario, Canada
Questions & answers
Do participants get paid in this trial?
This listing doesn't specify compensation. Many trials still reimburse travel or offer a stipend, so it's worth asking the study team when you connect.
Is it free to join, and do I need insurance?
Searching and applying through BridgeMD is free. In clinical trials the study-related treatment and visits are generally provided at no cost to you. You usually don't need insurance to take part - confirm specifics with the study team.
How long does this study last?
The listing doesn't state an exact length. The study team walks you through the schedule and number of visits before you decide to enroll.
Who can join this trial?
This study is enrolling all sexes, 6 years to 18 years. The study team makes the final eligibility decision.
Where is this trial taking place?
Study sites include Ottawa, Ontario, Canada. Enter your location above to see the nearest site and check your eligibility.
Explore other conditions
BridgeMD is an information and trial-matching tool - not medical advice, and not the study sponsor. Details come from ClinicalTrials.gov; the study team decides eligibility.