BridgeMD
New treatment option for Infantile Spinal Muscular Atrophy
Official title Test of Aquatic Mobility of SMA Infants
ClinicalTrials.gov ID: NCT06152302
What this study is testing
- What it's testing
- Spinal muscular atrophy (SMA) is a genetic neurodegenerative disease impacting spinal cord motor neurons, leading to motor and respiratory issues and, ultimately, death. With emerging therapies, a need arises to enhance motor function assessment in severely hypotonic infants (SMA type 1) as traditional scales on examination tables lack completeness due to gravity's influence.
A plain-language read of the study's public ClinicalTrials.gov listing. The study team confirms the details.
Who can take part
Ages up to 12
You may be able to join if
- Infants with muscle weakness (commonly referred to as floppy babies):
- Confirmed diagnosis of SMA through gene mutation or deletion (SMN1 gene).
- Receiving standard care.
- Age less than 12 years and a height of less than 90 cm at the time of inclusion.
- Patients enrolled in a social security scheme.
You likely can't join if
- Patients presenting with lesions in the spinal cord or conditions affecting the cardiorespiratory system.
- Patients covered under the French Aid in Health for Foreign People program (AME).
See the full eligibility criteria
- Infants with muscle weakness (commonly referred to as floppy babies):
- Confirmed diagnosis of SMA through gene mutation or deletion (SMN1 gene).
- Receiving standard care.
- Age less than 12 years and a height of less than 90 cm at the time of inclusion.
- Patients enrolled in a social security scheme.
- Informed consent signed by both parents of the child and the investigator.
- Patients presenting with lesions in the spinal cord or conditions affecting the cardiorespiratory system.
- Patients covered under the French Aid in Health for Foreign People program (AME).
The study team makes the final eligibility decision.
Where it's taking place
- Garches, France
Questions & answers
Do participants get paid in this trial?
This listing doesn't specify compensation. Many trials still reimburse travel or offer a stipend, so it's worth asking the study team when you connect.
Is it free to join, and do I need insurance?
Searching and applying through BridgeMD is free. In clinical trials the study-related treatment and visits are generally provided at no cost to you. You usually don't need insurance to take part - confirm specifics with the study team.
How long does this study last?
The listing doesn't state an exact length. The study team walks you through the schedule and number of visits before you decide to enroll.
Who can join this trial?
This study is enrolling all sexes, up to 12 months. The study team makes the final eligibility decision.
Where is this trial taking place?
Study sites include Garches, France. Enter your location above to see the nearest site and check your eligibility.
Explore other conditions
BridgeMD is an information and trial-matching tool - not medical advice, and not the study sponsor. Details come from ClinicalTrials.gov; the study team decides eligibility.