Authorised Therapeutic confirmatory (Phase III) X-Linked Retinitis Pigmentosa caused by mutations in the RPGR gene

Long Term Follow-Up study of Gene Therapy Trial for Patients with Retinitis Pigmentosa (progressive reduction in vision) due to a gene defect on Chromosome X.

EU CTIS ID: 2024-511411-25-00

What this study is testing

To assess the long-term safety and tolerability of AAV5-hRKp.RPGR in individuals with RPGR-XLRP.

  • Therapeutic confirmatory (Phase III)

A plain-language read of the study's public EU CTIS listing. The study team confirms the details.

Who can take part

You may be able to join if

  • 1.Previously completed participation in Study MGT-RPGR-021.
  • 2.Must reconfirm that he or she understands the purpose of, and procedures required for, the study and is willing to participate in the study.

You likely can't join if

  • There are no specific exclusion criteria.

The study team makes the final eligibility decision.

Where it's taking place

  • United Kingdom
  • United States
  • Israel
  • Canada
  • Switzerland

Questions & answers

Do participants get paid in this trial?

This listing doesn't specify compensation. Many trials still reimburse travel or offer a stipend, so it's worth asking the study team when you connect.

Is it free to join, and do I need insurance?

Searching and applying through BridgeMD is free. In clinical trials the study-related treatment and visits are generally provided at no cost to you. You usually don't need insurance to take part - confirm specifics with the study team.

How long does this study last?

The listing doesn't state an exact length. The study team walks you through the schedule and number of visits before you decide to enroll.

Who can join this trial?

This study is enrolling all sexes, 0-17 years, 18-64 years. The study team makes the final eligibility decision.

Where is this trial taking place?

Study sites include United Kingdom; United States; Israel; Canada; Switzerland. Enter your location above to see the nearest site and check your eligibility.

Explore other conditions

BridgeMD is an information and trial-matching tool - not medical advice, and not the study sponsor. Details come from EU CTIS; the study team decides eligibility.